Long-term benefit of enzyme replacement therapy with alglucosidase alfa in adults with Pompe disease: prospective analysis from the French Pompe Registry.

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Semplicini, C. | de Antonio, M. | Taouagh, N. | Béhin, A. | Bouhour, F. | Echaniz-Laguna, A. | Magot, A. | Nadaj-Pakleza, A. | Orlikowski, D. | Sacconi, S. | Salort-Campana, E. | Solé, G. | Tard, Celine | Zagnoli, F. | Jean-Yves, H. | Hamroun, D. | Laforêt, P. | Attarian, S. | Aubé-Nathier, A. C. | Arrassi, A. | Bassez, G. | Bedat-Millet, A. L. | Bouibede, F. | Boyer, F. C. | Caillaud, C. | Canal, A. | Carlier, R. Y. | Chanson, J. B. | Chapon, F. | Cintas, P. | Deibener-Kaminsky, J. | Demurger, F. | Desnuelle, C. | Durieu, I. | Eymard, B. | Feasson, L. | Fournier, M. | Froissart, R. | Furby, A. | Garcia, P. Y. | Germain, D. P. | Ghorab, K. | Morales, R. J. | Krim, E. | Labauge, P. | Lacour, A. | Lagrange, E. | Lefeuvre, C. | Leguy-Seguin, V. | Leonard-Louis, S. | Magy, L. | Masseau, A. | Michaud, M. | Minot-Myhié, M. C. | Nicolas, G. | Nollet, S. | Not, A. | Noury, J. B. | Ollivier, G. | Péréon, Y. | Perez, Thierry | Perniconi, B. | Piraud, M. | Petiot, P. | Pouget, J. | Praline, J. | Prigent, H. | Renard, D. | Spinazzi, M. | Stojkovic, T. | Taithe, F. | Tiffreau, Vincent | Vincent, D.

Edité par CCSD ; Springer Verlag -

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